Margarida R G Maia

Specific mutations in the DMD gene influence how long patients retain the ability to walk, even when treated with corticosteroids, a study says.

The case is reported of a young woman who began having DMD symptoms before getting pregnant, allowing her to receive genetic counseling.

Entrada plans to initiate clinical testing of ENTR-601-44 in Duchenne MD patients amenable to exon 44 skipping later this year.